These results are published in the American Journal of Respiratory Cell and Molecular Biology. Cystic fibrosis is the most ..

An in vitro study of PTC124, a drug in clinical trials for the treatment of cystic fibrosis and several other genetic disorders, has some scientists wondering whether the molecule works the way its ...

Two independent research teams have used single-cell RNA sequencing to generate detailed molecular atlases of mouse and human ... type that expresses high levels of the gene mutated in cystic fibrosis ...

The present study reveals genetic mechanisms in the development of liver fibrosis and offers new therapeutic possibilities to ...

The Massachusetts-based biotech plans to use the funds to push its candidates into mid-stage clinical trials in a space ...

Engelhardt, Ph.D., is highly regarded for his research focused on the molecular basis of ... and gene editing pathogenesis cystic fibrosis related diabetes the study of airway stem cell niches, the ...

In a new study, Yale researchers have started to uncover what happens at the cellular and molecular ... losing lipids, fibrosis still occurred and was actually more pronounced. The finding suggests ...

In December, the FDA approved Vertex’s vanzacaftor, tezacaftor and deutivacaftor (Alyftrek) for the treatment of cystic fibrosis in patients with at least one F508del mutation or another ...