Friedreich’s ataxia and more general forms of hereditary ataxias. The most common symptoms of the disease "are balance and walking difficulties, clumsiness, vision changes, speech difficulties ...

But all that time, she had been reading up on my symptoms on the internet - and came across Friedreich's Ataxia. She was convinced that is what I had and, sure enough, when the results came back ...

In too many cases, this disease is diagnosed many years after the first symptoms have appeared. The follow-up of patients with Friedreich ataxia involves pediatric and adult neurologists ...

PTC Therapeutics could boost revenue with vatiquinone for Friedreich's ataxia. Find out why PTCT stock is poised for growth ...

There are several current treatment options for Friedreich's ataxia, or FA as I'll call it for the rest of this time. The most important is what we had before the approval of any drugs.

After getting a green light from the European Commission, Biogen’s Skyclarys is the first approved medicine for the inherited neurological disease Friedreich’s ataxia (FA) in the EU.

The Food and Drug Administration (FDA) has accepted for Priority Review the New Drug Application (NDA) for vatiquinone for the treatment of children and adults living with Friedreich ataxia (FA).

Biogen’s Skyclarys is on course to becoming the first approved medicine for the inherited neurological disease Friedreich’s ataxia (FA ... results in a range of symptoms that worsen over ...

Solid Biosciences' SGT-212, dual-route gene therapy for Friedreich’s ataxia, receives FDA Fast ... addressing the disease's neurological and cardiac symptoms. The FDA's Fast Track designation ...

"We are excited to be one step closer to bringing an approved therapy to all patients with Friedreich's ataxia," said Matthew ... and neuromuscular disease symptoms. About MOVE-FA MOVE-FA was ...