Taysha Gene Therapies shares fall after regaining full rights to Rett syndrome drug TSHA-102 and finalizing FDA alignment for ...

The Big Pharma’s window to take up exclusive rights to Taysha’s lead asset, dubbed TSHA-102, has officially closed, according ...

David Lieberman, MD, PhD: Some long-term complications in Rett syndrome include scoliosis. Features of scoliosis often appear by age 12. They can get quite severe as the girl is going through her ...

An expert discusses the current treatment landscape of Rett syndrome including the goals of treatment and implications for utilization management strategies with the disease. David Lieberman, MD, PhD: ...

The Valdez family invites the community to join them on Oct. 26 at Starlight Meadow, 7157 Shoe Road, Burlington, for a ...

Rett syndrome is one of the rare genetic disorders and almost exclusively affects girls. In Germany, an estimated 5,000 people are affected, with about 50 new cases each year. A disturbing sign: After ...

Rett syndrome is a neurodevelopmental disorder that primarily affects girls, most of whom have mutations in the transcription regulatory gene MECP2. However, mutations in MECP2 also have been ...

The Canadian Rett Syndrome Coalition - comprising the Rett Syndrome Society of British Columbia (RSSBC), Rett Syndrome Society of Alberta (RSSA), Saskatchewan Rett Syndrome Association (SRSA), ...

Richard Engel, chief foreign correspondent for NBC News, announced on Thursday that his six-year-old son Henry had passed away from a rare neurological disorder. “Our beloved son Henry passed away,” ...