Rett syndrome is one of the rare genetic disorders and almost exclusively affects girls. In Germany, an estimated 5,000 people are affected, with about 50 new cases each year. A disturbing sign: After ...

SAN FRANCISCO--(BUSINESS WIRE)--Herophilus announced today that in vivo studies underway of its lead candidate HRP-12975 are funded in part by the Rett Syndrome Research Trust (RSRT). HRP-12975 is the ...

The Food and Drug Administration on Friday approved the first treatment for Rett syndrome, a genetic disease mostly affecting girls that causes severe neurologic impairments, robbing them of the ...

The Upstate New York Reverse Rett committee is calling on the community to support its 4th annual Reverse Rett Upstate New York Fall Festival, an event dedicated to raising funds for Rett Syndrome ...

ST. LOUIS, Mo. - Anushka Shah, who has her sights set on college, just graduated high school at 19-years-old with a 3.75 GPA. Anushka has Rett syndrome and is unable to speak or use her hands. She ...

UAB will study a drug originally developed for Parkinson’s disease that may help reduce breath holding in patients with Rett syndrome. Pediatric neurologist Alan Percy, M.D., is a leading clinician ...

Taysha’s TSHA-102 shows 100% response in Rett, with FDA Breakthrough status and strong trial design supporting BLA hopes. Read why TSHA stock is a buy.

Neurogene has dropped plans to keep studying the high dose of its Rett syndrome gene therapy because of an adverse event that has left a patient in critical condition. The discontinuation has pushed ...

After a patient died following a high dose of Neurogene’s Rett syndrome gene therapy candidate, the biotech is sharing details about the event and the new safety protocols being incorporated into the ...

BENGALURU: Awareness about rare diseases can sometimes prevent serious conditions from being overlooked. One such condition is Rett Syndrome, a rare neurological disorder that many people aren’t ...