From 2008 to 2023, there has been a significant decrease in cystic fibrosis mortality rates and a significant rise in sickle ...
Painful symptoms of sickle-cell disease begin within the first year of life. Hydroxyurea (hydroxycarbamide) has been shown to reduce pain in adults (N Engl J Med. 1995;332:1317-1322) and has been ...
Mitapivat significantly boosted hemoglobin in SCD patients over one year, paving the way for potential FDA submission for ...
You might have wondered why some people with sickle cell disease seem to live relatively normal lives while others spend half their time in the hospital writhing in agony from pain crises. It’s the ...
LONDON--(BUSINESS WIRE)--MiNA Therapeutics Limited, the pioneer in small activating RNA (RNAa) therapeutics, today presented new pre-clinical data for its lead RNA activation program for the treatment ...
SHANGHAI, Aug. 26, 2025 /PRNewswire/ -- CorrectSequence Therapeutics Co., Ltd. (Correctseq), a clinical-stage biotechnology company pioneering transformer Base Editing (tBE) technology for the ...
Marissa Johanna Maria Traets Bridging Pathophysiology and Therapeutic Targets in Sickle Cell Disease dr. M.A.E. Rab ...
The launch of BIRSA 101 marks a major breakthrough in CRISPR gene-editing technology, positioning India to deliver affordable ...
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