Cellarity, a clinical-stage biotechnology company developing Cell State-Correcting therapies through integrated multi-omics and AI modeling, today announced the presentation of new preclinical data on ...
Patients who underwent hematopoietic cell transplantation for sickle cell disease saw high rates of survival without disease ...
Painful symptoms of sickle-cell disease begin within the first year of life. Hydroxyurea (hydroxycarbamide) has been shown to reduce pain in adults (N Engl J Med. 1995;332:1317-1322) and has been ...
SHANGHAI, Aug. 26, 2025 /PRNewswire/ -- CorrectSequence Therapeutics Co., Ltd. (Correctseq), a clinical-stage biotechnology company pioneering transformer Base Editing (tBE) technology for the ...
Patients who underwent hematopoietic cell transplantation for sickle cell disease saw high rates of survival without disease ...
LONDON--(BUSINESS WIRE)--MiNA Therapeutics Limited, the pioneer in small activating RNA (RNAa) therapeutics, today presented new pre-clinical data for its lead RNA activation program for the treatment ...
For years, my family struggled to understand the constant, mysterious pain my younger sister and I endured. Her cries were so frequent that she earned the nickname “Holly” because she was always ...
A study assessing the real-world commercial roll-out of gene therapies for sickle cell disease and beta thalassemia offers ...
During September, numerous national and local organizations, along with diverse communities, individuals affected by sickle cell disease, their families, healthcare providers, and dedicated advocates ...