As a parent with a child who has sickle cell disease, you are always on high alert. The “what if” stays with me, as it ...
Mitapivat significantly boosted hemoglobin in SCD patients over one year, paving the way for potential FDA submission for approval.
Painful symptoms of sickle-cell disease begin within the first year of life. Hydroxyurea (hydroxycarbamide) has been shown to reduce pain in adults (N Engl J Med. 1995;332:1317-1322) and has been ...
SHANGHAI, Aug. 26, 2025 /PRNewswire/ -- CorrectSequence Therapeutics Co., Ltd. (Correctseq), a clinical-stage biotechnology company pioneering transformer Base Editing (tBE) technology for the ...
LONDON--(BUSINESS WIRE)--MiNA Therapeutics Limited, the pioneer in small activating RNA (RNAa) therapeutics, today presented new pre-clinical data for its lead RNA activation program for the treatment ...
From 2008 to 2023, there has been a significant decrease in cystic fibrosis mortality rates and a significant rise in sickle ...
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Uganda: JCRC Seeks Shs14bn to Establish Uganda's First Bone-Marrow Treatment Centre for Sickle Cell Patients
The Joint Clinical Research Center (JCRC) has launched an urgent appeal for $4 million (about Shs14 billion) to build Uganda's first dedicated facility for treating Sickle Cell Disease and blood ...
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