A Phase 1b trial shows the higher dose of pociredir boosts fetal hemoglobin levels in adults with sickle cell disease.

SHANGHAI, Aug. 26, 2025 /PRNewswire/ -- CorrectSequence Therapeutics Co., Ltd. (Correctseq), a clinical-stage biotechnology company pioneering transformer Base Editing (tBE) technology for the ...

Painful symptoms of sickle-cell disease begin within the first year of life. Hydroxyurea (hydroxycarbamide) has been shown to reduce pain in adults (N Engl J Med. 1995;332:1317-1322) and has been ...

Patients who underwent hematopoietic cell transplantation for sickle cell disease saw high rates of survival without disease ...

Patients who underwent hematopoietic cell transplantation for sickle cell disease saw high rates of survival without disease ...

LONDON--(BUSINESS WIRE)--MiNA Therapeutics Limited, the pioneer in small activating RNA (RNAa) therapeutics, today presented new pre-clinical data for its lead RNA activation program for the treatment ...

Cellarity, a clinical-stage biotechnology company developing Cell State-Correcting therapies through integrated multi-omics and AI modeling, today announced the presentation of new preclinical data on ...

A study assessing the real-world commercial roll-out of gene therapies for sickle cell disease and beta thalassemia offers ...

Five studies presented at the 67th American Society of Hematology (ASH) Annual Meeting and Exposition reveal new ...

For years, my family struggled to understand the constant, mysterious pain my younger sister and I endured. Her cries were so frequent that she earned the nickname “Holly” because she was always ...