Former Little Mix star Jesy Nelson revealed on social media that her twin girls have been diagnosed with a rare genetic ...

Spinal muscular atrophy explained after Jesy Nelson reveals her twins’ diagnosis - The singer shared an emotional update ...

Little Mix alum Jesy Nelson opened up in an emotional video Jan. 4 about her twin daughters’ Spinal Muscular Atrophy Type 1 diagnosis, a life-threatening disease that leads to severe muscle weakness.

Spinal muscular atrophy is a genetically inherited disorder that causes muscle weakness. Adults can get spinal muscular atrophy, but it’s rare in adults and progresses slowly. It doesn’t typically ...

Spinal muscular atrophy (SMA) is a genetic neuromuscular disease affecting specialized nerve cells that control voluntary muscle movement, according to the Muscular Dystrophy Association (MDA). It can ...

Spinal and bulbar muscular atrophy (SBMA), also known as Kennedy’s disease, is a rare genetic disorder. It affects certain nerve cells in the spinal cord and the brainstem. “Bulbar” refers to a ...

Spinal muscular atrophy with respiratory distress (SMARD) is a rare genetic condition that typically affects infants and children. It causes muscle weakness and breathing problems. Spinal muscular ...

Jason Mast is a general assignment reporter at STAT focused on the science behind new medicines and the systems and people that decide whether that science ever reaches patients. You can reach Jason ...

A Prescription Drug User Fee Act target date of September 22, 2025 has been set for the application. The Food and Drug Administration (FDA) has accepted for Priority Review the Biologics License ...

Panelists discuss how spinal muscular atrophy is an autosomal recessive genetic disease affecting motor neurons with 3 currently approved disease-modifying therapies that restore SMN protein ...