Cystic fibrosis transmembrane conductance regulator gene rearrangements were searched ... Three mutations were found as complex alleles (two or three sequence alterations associated in cis on ...

No doubt 2025 will usher in many more advances in CRISPR therapies, thanks to the FDA’s new Platform Technology Designation ...

On Friday, in a significant policy shift, the National Institutes of Health (NIH) announced immediate cuts to grants ...

In this series, ‘Genomics 101’, we go back to basics and explore some of the most important topics in genomics. In this blog, we explain the term ...

Precision medicine is revolutionizing healthcare, and these genomic stocks are leading the way. Therefore, as this sector ...

Based on this, we have developed a new approach to enhance the efficiency of rAAV-mediated gene expression ... of therapeutic transgenes (such as cystic fibrosis transmembrane conductance ...

Detailed price information for 4D Molecular Therapeutics Inc (FDMT-Q) from The Globe and Mail including charting and trades.

These work by binding to specific mRNA sequences in order to modify gene expression. By correcting faulty RNA ... For the lung disease cystic fibrosis, Vertex Pharmaceuticals has an mRNA medicine, ...

Did you see this? Nearly 1 in 10 Americans have asthma. Here's what causes it.

The genetic disorder cystic fibrosis is unique because it can cause both breathing and digestive problems. Some 40,000 people in the U.S. currently have it, "though this is likely an ...