Today, Sammy is 17 years old and working hard to be able to walk across the stage at her high school graduation next spring. Whether kids like Sammy can achieve their dreams depends on whether ...

“Typical tactics used by bullies include, but are not limited to: Slamming objects…” ...

Rett syndrome is one of the rare genetic disorders and almost exclusively affects girls. In Germany, an estimated 5,000 people are affected, with about 50 new cases each year. A disturbing sign: After ...

An announcement from Neurogene ( ($NGNE) ) is now available. On October 9, 2025, Neurogene Inc. announced the completion of discussions with the ...

New preclinical data at ESGCT Congress highlight NGN-401 best-in-class potential and add to body of evidence that ICV administration is superior to IT-L in reaching key brain regions underlying Rett ...

Taysha’s TSHA-102 shows 100% response in Rett, with FDA Breakthrough status and strong trial design supporting BLA hopes. Read why TSHA stock is a buy.

Child death rates in Kern County over the past five years recorded significant disparities compared to the statewide and ...

Breakthrough Therapy designation granted based on FDA’s review of available clinical evidence of safety and efficacy from all 12 patients treated in Part A of the REVEAL Phase 1/2 trials Finalized FDA ...

(RTTNews) - Biotechnology company Taysha Gene Therapies, Inc. (TSHA) announced the U.S. Food and Drug Administration (FDA) has granted Breakthrough Therapy designation to TSHA-102, an intrathecally ...

Editor's Note: The story has been amended to more accurately reflect Pima County statistics on overdose deaths. Nationally, overdose deaths fell by about 27% in 2024. That's the largest one-year ...