A specialist from Oman, located at the crossroads of Africa and Asia, explains that his nation serves as a microcosm when it ...

Vascarta is a healthspan-focused, clinical-stage biopharmaceutical company pioneering topical/transdermal therapies to ...

SICKLE cell disease is a disease that affects people across the world. This disease affects a wide range of nations and ethnic groups. It is a genetic disorder that results from receiving the sickle ...

Announced encouraging results in July 2025 from the 12 mg dose cohort of the Phase 1b PIONEER trial of pociredir in sickle cell disease (SCD) ― ...

Genetix Biotherapeutics Inc. today announced that an analysis of recent patient experience data from the commercial implementation of LYFGENIAtm and ZYNTEGLOtm in the U.S. has been selected for oral ...

Agios Pharmaceuticals, Inc. (Nasdaq: AGIO), a commercial-stage biopharmaceutical company focused on delivering innovative medicines for patients with rare diseases, today announced that new data on ...

Vascarta Inc., a healthspan focused, clinical stage biopharmaceutical company advancing safe, patient friendly ...

In a world-first trial, scientists used a one-off CRISPR gene edit to switch off a liver “fat brake” gene, slashing stubborn ...

Traditional medications are synthesized through chemical reactions, whereas biologics are derived from and reproduced, at ...

Dr Drews Adade reveals how bias in medical research leads to missed diagnoses, unequal treatment, and preventable deaths ...

Sanofi's Wayrilz recommended for EU approval by the CHMP to treat immune thrombocytopenia Recommendation based on LUNA 3 phase 3 study demonstrating rapid and durable platelet response and significant ...

A Phase 1b clinical trial testing pociredir in adults with sickle cell disease has completed enrollment of its high-dose group.