LIVINGSTON, Texas (AP) — Robert Roberson was calm and hopeful as he pondered his mortality and whether he could again avoid becoming the first person in the U.S. executed for a murder conviction tied ...
Taysha Gene Therapies, Inc.’s lead asset is TSHA-102. This is an intrathecal AAV9 gene therapy for Rett with a 100% Phase 1/2 responder rate and favorable safety. The FDA granted it a Breakthrough ...
Breakthrough Therapy designation granted based on FDA’s review of available clinical evidence of safety and efficacy from all 12 patients treated in Part A of the REVEAL Phase 1/2 trials Finalized FDA ...
Oral vitamin B12 supplements may offer an additional way to prevent hand-foot syndrome, a common side effect of chemotherapy with capecitabine, a clinical trial suggested. The phase 3 trial, conducted ...
Rett syndrome is one of the rare genetic disorders and almost exclusively affects girls. In Germany, an estimated 5,000 people are affected, with about 50 new cases each year. A disturbing sign: After ...
SPEIGLETOWN, N.Y. (NEWS10) — Families across the Capital Region came together on Saturday to raise money and awareness for a rare neurological disorder called Rett Syndrome. Saturday was the Reverse ...
Puppies and kittens could have anyone wrapped around their paws in a matter of moments, but they aren't the only baby animals that raise the bar when it comes to cuteness. On September 17, Fallen Oak ...
The Upstate New York Reverse Rett committee is calling on the community to support its 4th annual Reverse Rett Upstate New York Fall Festival, an event dedicated to raising funds for Rett Syndrome ...
Researchers led by UC Davis Health scientist Sanchita Bhatnagar have developed a promising gene therapy that could treat Rett syndrome. The therapy works on reactivating healthy but silent genes ...
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