Spinraza was linked to changes in CSF biomarkers in SMA, some of which were associated with motor gains, but more research is ...

Columnist Sherry Toh pushes back against narratives that blame parents for a child's disability, and instead thanks her ...

As columnist Helen Baldwin prepares to celebrate the 29th birthday of her son, who died from SMA in 1997, she welcomes a new ...

Evidence-based guidelines have been developed for newborn screening, diagnosis, and early management of SMA in Australia and ...

Caregiving can involve multitasking, but columnist Connie Chandler asks what do you do when your caregiver is better at one ...

SMA newborn screening may help children start treatment earlier, supporting better independence and daily function at school ...

The FDA has accepted Scholar Rock's application for regulatory approval of apitegromab for SMA and is expected to have its ...

Columnist Ari Anderson shares how his home-care nurses help to provide him with two things that are vital while living with ...

Children with SMA diagnosed via newborn screening programs typically start treatment earlier and reach more motor milestones, ...

Leaning too far into joy or too deeply into sorrow is unrealistic, writes columnist Connie Chandler, who instead finds ...

U.K. experts developed consensus guidance to support earlier hip monitoring and individualized care decisions for children ...