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0:20
YouTube
California Institute for Regenerative Medicine
Rare Disease Webinar - Stephanie Cherqui, PhD
What started as discovery research to better understand cystinosis has grown into a promising stem cell-based genetic therapy with broader potential. UCSD's Dr. Stephanie Cherqui's research is an example of how progress in one rare disease may help accelerate treatments for others: https://bit.ly/4uB8xvv
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